Families of SMA and Nationwide Children's Announce Multi-Million Dollar Award From NINDS to Advance CNS Gene Therapy for Spinal Muscular Atrophy
March 13, 2013 13:12 ET | Families of SMA
ELK GROVE VILLAGE, Ill., March 13, 2013 (GLOBE NEWSWIRE) -- Nationwide Children's Hospital (Columbus, OH) and Families of Spinal Muscular Atrophy (Elk Grove Village, IL) announce the award of a...
Pfizer Licenses Families of Spinal Muscular Atrophy Quinazoline Drug Program From Repligen
January 03, 2013 09:31 ET | Families of SMA
ELK GROVE VILLAGE, Ill., Jan. 3, 2013 (GLOBE NEWSWIRE) -- Repligen Corporation announced today that it has entered into an exclusive worldwide licensing agreement with Pfizer Inc. to advance...
Families of Spinal Muscular Atrophy Committed $2.5 Million to Funding SMA Research in 2012
December 31, 2012 10:06 ET | Families of SMA
ELK GROVE VILLAGE, Ill., Dec. 31, 2012 (GLOBE NEWSWIRE) -- Families of SMA is dedicated to creating a treatment and cure for Spinal Muscular Atrophy by funding and advancing a comprehensive research...
Families of Spinal Muscular Atrophy Awards $710,000 for Basic Research to Identify New and More Effective Approaches for SMA Therapies
December 28, 2012 10:07 ET | Families of SMA
ELK GROVE VILLAGE, Ill., Dec. 28, 2012 (GLOBE NEWSWIRE) -- Families of SMA is dedicated to creating a treatment and cure for Spinal Muscular Atrophy by funding and advancing a comprehensive research...
Repligen Initiates Phase 1b Trial of RG3039 for Spinal Muscular Atrophy Licensed From Families of SMA
September 26, 2012 16:17 ET | Families of SMA
ELK GROVE VILLAGE, Ill., Sept. 26, 2012 (GLOBE NEWSWIRE) -- Repligen Corporation has initiated a Phase 1b clinical study of RG3039, a novel small molecule drug candidate for the potential treatment of...
Families of SMA Announces $1.4 Million Planned for Next Round of Spinal Muscular Atrophy Research Funding
June 07, 2012 15:13 ET | Families of SMA
ELK GROVE VILLAGE, Ill., June 7, 2012 (GLOBE NEWSWIRE) -- Families of Spinal Muscular Atrophy (FSMA) is dedicated to creating a treatment and cure for Spinal Muscular Atrophy (SMA) by funding and...
Families of SMA Announces $700,000 Funding for Novel Drug Program at Newly Created California Institute for Biomedical Research
May 10, 2012 15:44 ET | Families of SMA
ELK GROVE VILLAGE, Ill., May 10, 2012 (GLOBE NEWSWIRE) -- This new program will focus on optimizing small molecule drug candidates which increase the SMA back-up gene in order to make them ready for...
Families of SMA Awards New Funding to Advance a CNS Delivered Gene Therapy for Spinal Muscular Atrophy
May 02, 2012 16:14 ET | Families of SMA
ELK GROVE VILLAGE, Ill., May 2, 2012 (GLOBE NEWSWIRE) -- Families of SMA is pleased to announce the award of up to $750,000 for an important new grant to Dr. Brian Kaspar at Nationwide Children's...
Repligen Reports Positive Results From Phase 1 Clinical Trial for Spinal Muscular Atrophy (SMA)
April 25, 2012 10:36 ET | Families of SMA
ELK GROVE VILLAGE, Ill., April 25, 2012 (GLOBE NEWSWIRE) -- Repligen Corporation (Nasdaq:RGEN) today announced positive results from a Phase 1 study to evaluate the pharmacokinetic (PK) and safety...
Update on the Spinal Muscular Atrophy Drug Development Pipeline From Families of SMA
January 19, 2012 10:07 ET | Families of SMA
ELK GROVE VILLAGE, Ill., Jan. 19, 2012 (GLOBE NEWSWIRE) -- Developing new therapies to treat and ultimately cure SMA is the driving force behind Families of SMA. To achieve this goal, Families of SMA...