-- Preparations Underway for Late-Stage Development in Hemophilia B
-- Three Clinical-Stage Programs by 2018 Including One Pivotal and Two Proof-of-Concept Studies
-- Company Strengthened Following Strategic Review and New Executive Leadership
LEXINGTON, Mass. and AMSTERDAM, the Netherlands, Jan. 09, 2017 (GLOBE NEWSWIRE) -- uniQure N.V. (NASDAQ:QURE), a leader in human gene therapy, today announced its key corporate initiatives for 2017 and vision for 2018 following the completion of a company-wide strategic review late last year that refocuses its pipeline, streamlines operations, improves its financial position and enhances overall execution and shareholder value. uniQure management is meeting with investors and analysts this week in conjunction with the 35th Annual J.P. Morgan Healthcare Conference taking place in San Francisco. An updated corporate presentation is posted to the investor page of the Company’s website, www.uniqure.com.
“As we begin 2017, we expect each of our core programs to achieve important milestones that will bring us closer to delivering life-transforming gene therapies for patients,” stated Matthew Kapusta, chief executive officer of uniQure. “Our key focus is to rapidly advance our hemophilia B program into late-stage development. By 2018, we expect to have three clinical-stage programs, including a pivotal study for AMT-060 in hemophilia B, and two clinical proof-of-concept studies for congestive heart failure and Huntington’s disease. We believe our financial position is strong and capable of funding the accomplishment of these objectives.”
Recent Accomplishments
Key Corporate Initiatives for 2017
uniQure had approximately €140 million ($158 million) in cash and cash equivalents as of September 30, 2016, which is expected to fund operations into 2019.
About uniQure
uniQure is delivering on the promise of gene therapy – single treatments with potentially curative results. We are leveraging our modular and validated technology platform to rapidly advance a pipeline of proprietary and partnered gene therapies to treat patients with hemophilia, Huntington’s disease and cardiovascular diseases. www.uniQure.com.
uniQure Forward-Looking Statements
This press release contains forward-looking statements. All statements other than statements of historical fact are forward-looking statements, which are often indicated by terms such as "anticipate," "believe," "could," "estimate," "expect," "goal," "intend," "look forward to", "may," "plan," "potential," "predict," "project," "should," "will," "would" and similar expressions. Forward-looking statements are based on management's beliefs and assumptions and on information available to management only as of the date of this press release. These forward-looking statements include, but are not limited to, statements regarding the implementation and effects of the Company’s new strategic and organizational changes, the development of our gene therapy product candidates, the success of our collaborations and the risk of cessation, delay or lack of success of any of our ongoing or planned clinical studies and/or development of our product candidates. Our actual results could differ materially from those anticipated in these forward-looking statements for many reasons, including, without limitation, risks associated with corporate reorganizations and strategic shifts, collaboration arrangements, our and our collaborators’ clinical development activities, regulatory oversight, product commercialization and intellectual property claims, as well as the risks, uncertainties and other factors described under the heading "Risk Factors" in uniQure’s 2015 Annual Report on Form 20-F filed with the Securities and Exchange Commission on April 4, 2016. Given these risks, uncertainties and other factors, you should not place undue reliance on these forward-looking statements, and we assume no obligation to update these forward-looking statements, even if new information becomes available in the future.