American Kidney Fund
American Kidney Fund Survey Underscores Need to Expand Testing for Chronic Kidney Disease and Increase Awareness of Rare Kidney Diseases
April 07, 2022 09:00 ET | American Kidney Fund
ROCKVILLE, Md., April 07, 2022 (GLOBE NEWSWIRE) -- The American Kidney Fund (AKF) today released survey findings that provide new insights on the level of awareness among health care providers about...
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FDA approves Novartis Vijoice® (alpelisib) as first and only treatment for select patients with PIK3CA-Related Overgrowth Spectrum (PROS)
April 05, 2022 20:29 ET | Novartis Pharma AG
Vijoice is first approved treatment to specifically address the root cause of PROS conditions in select patients 2 years of age and older1 PROS is a spectrum of rare conditions and is characterized by...
Global Liver Institu
Global Liver Institute Leads Second Annual Rare Liver Diseases Month
February 01, 2022 10:41 ET | Global Liver Institute
Washington, DC, USA, Feb. 01, 2022 (GLOBE NEWSWIRE) -- Global Liver Institute (GLI), a patient-led liver health nonprofit operating globally, is proud to announce today the launch of its second...
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CURATIVE BIOTECHNOLOGY ANNOUNCES DR. CATHERINE SOHN AS SPECIAL ADVISOR TO BOARD AND CEO
October 12, 2021 10:12 ET | Curative Biotechnology, Inc. 
Dr. Sohn to Oversee Development of Next Gen COVID-19 Vaccine to Treat Kidney Failure Patients, Late-Stage Rabies Therapeutic and Age-related Macular Degeneration Boca Raton, FL, Oct. 12, 2021 ...
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The Oligonucleotide Therapeutics Society Celebrates Another Remarkable Annual Meeting
October 09, 2021 12:00 ET | The Oligonucleotide Therapeutics Society
SAN DIEGO, Oct. 09, 2021 (GLOBE NEWSWIRE) -- The Oligonucleotide Therapeutics Society's 17th Annual Meeting was held virtually the second year in a row and was once again phenomenally successful....
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Fortress Biotech Announces Receipt of Notice of Option Exercise from AstraZeneca to Fully Acquire Caelum Biosciences, a Company Founded by Fortress Biotech
September 29, 2021 07:00 ET | Fortress Biotech, Inc.
Option exercise triggers upfront payment of approximately $150 million to Caelum shareholders, of which approximately $64 million is payable to Fortress Biotech1 AstraZeneca intends to advance and...
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Novartis announces positive FDA Advisory Committee recommendation for use of Entresto® to treat patients with HFpEF
December 15, 2020 19:17 ET | Novartis International AG
The Committee voted 12 to 1 that the data presented support the use of Entresto in treatment of patients with heart failure with preserved ejection fraction (HFpEF)Potential Q1 2021 sNDA approval...
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Axiom will be Presenting and Exhibiting at Clinical Trials in Rare Diseases 2020: A Virtual Event
December 02, 2020 11:36 ET | Axiom Real-Time Metrics Inc
TORONTO, Dec. 02, 2020 (GLOBE NEWSWIRE) -- Axiom Real-Time Metrics (“Axiom”), premier provider of unified eClinical solutions and services, is a presenting sponsor and exhibitor at Clinical Trials...
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AskBio and Selecta Biosciences Receive Orphan Drug Designation for MMA-101 to Treat Methylmalonic Acidemia
November 19, 2020 08:00 ET | Asklepios BioPharmaceutical, Inc.
RESEARCH TRIANGLE PARK, N.C. and WATERTOWN, Mass., Nov. 19, 2020 (GLOBE NEWSWIRE) -- Asklepios BioPharmaceutical, Inc. (AskBio) and Selecta Biosciences, Inc. (NASDAQ: SELB) today announced that the...
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Selecta Biosciences and AskBio Receive FDA Rare Pediatric Disease Designation for their Gene Therapy for Methylmalonic Acidemia
October 20, 2020 08:00 ET | Asklepios BioPharmaceutical, Inc.
WATERTOWN, Mass., and Research Triangle Park, N.C., Oct. 20, 2020 (GLOBE NEWSWIRE) -- Selecta Biosciences, Inc. (NASDAQ: SELB) and Asklepios BioPharmaceutical, Inc. (AskBio), today announced the...